US FDA Approves Mirum Rare Bone Drug

The US Food and Drug Administration has approved Mirum Pharmaceuticals drug to treat a rare bone disorder. The regulatory decision was announced on Friday.

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Mirum Pharmaceuticals Inc won United States Food and Drug Administration approval for its therapy targeting a rare bone disorder, the regulator announced on Friday afternoon. The clearance expands the company's rare-disease portfolio following clinical trials. Investors have closely watched the regulatory decision as a key revenue driver for the drugmaker.

Regulatory Milestone

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